Пенсионерку вместо лечения привязали к кровати в российской больнице

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She knew the eyes of the world were on her when her first mission launched in 1995.

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Now recovering, Manjit Sangha said her life changed in the space of a weekend

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尽管目前全球仅有5000名婴幼儿使用该药,但罕见病药物的高定价模式,叠加长期持续给药的治疗需求,让Vosoritide的商业表现持续走高。2025年,该药销售额达9.27亿美元,同比增长26%,是BioMarin的核心商业化增长引擎。